Biotechnology Landmark: the First CRISPR Medicine approved in the UK and USA
The Food and Drug Administration (FDA) has joined the UK medicines regulator and has approved the first CRISPR-Cas9 gene-editing therapy to treat sickle-cell disease [1]. UK expands approval to β-thalassemia. The approval of Casgevy, the therapy developed by Vertex and CRISPR Therapeutics, is the first [...]